Major Change for Rare Disease Treatments on Way, Signals MHRA
New paper sets out UK regulator's intentions to overhaul rulebook for rare disease therapies in UK New paper published today commits UK to major reform in rare therapies Bold new rulebook for rare therapies is being written, for publication next year ≈3.5 million people in UK affected by rare disease but only 5% of rare diseases have approved treatment MHRA reforms will speed up path for rare therapies from discovery to delivery The rulebook for rare disease therapies will be overhauled...
